Stay informed with the latest updates for the inheritable blood disorders community. Industry Spark Provides Trial Updates for Investigational Gene Therapy SPK-8011Aug 2, 2021 Industry FDA Places Clinical Hold on Sigilon’s Investigational Hemophilia TherapyJul 12, 2021 Industry BioMarin Presents Positive Safety and Efficacy Data for their…May 27, 2021 Industry Gene Therapy Trial Data Suggests Efficacy in the Presence of AntibodiesMay 25, 2021 Industry Gene Therapy Licensing Agreement Between uniQure and CSL Now in EffectMay 7, 2021 Industry uniQure Announces End of Clinical Hold on Hemophilia B Gene Therapy…Apr 27, 2021 Industry uniQure Announces Findings from HCC Case InvestigationMar 30, 2021 Industry Update to Hemlibra® (emicizumab-kxwh) USPIMar 12, 2021 Industry New Program Looks to Standardize Care for Patients with Rare DiseasesMar 2, 2021 Industry FDA Partially Rescinds Added Indications for Two FIX ProductsFeb 23, 2021 Industry Sanofi Revises Fitusiran Dosing Regimen to Mitigate Risk of Vascular…Feb 22, 2021 Industry Spark Announces Preliminary Data from Investigational Gene Therapy TrialFeb 19, 2021 Industry Octapharma Announces Final Results of Nuwiq® StudyFeb 19, 2021 Industry BioMarin Announces Positive Phase 3 Study Data for Valoctocogene…Jan 25, 2021 Industry FDA Puts Clinical Hold on uniQure's Hope B TrialDec 20, 2020 Pagination First page Previous page Page 1 Page 2 Page 3 Current page 4 Page 5 Page 6 Page 7 Page 8 Page 9 … Next page Last page