Stay informed with the latest updates for the inheritable blood disorders community.

Industry
Clinical Trial Gene Double Helix
BioMarin Announces FDA’s Extended Review of Investigational…
Mar 10, 2023
Industry
FDA Approval
uniQure Announces Published Trial Results for Approved Gene Therapy
Feb 27, 2023
Industry
FDA Approval
FDA Approves ALTUVIIIO™ for Hemophilia A Patients
Feb 24, 2023
Industry
Female Scientist Conducting Research in Lab Analyzing Data
Sanofi Announces New Efanesoctocog alfa Data Published in the NEJM
Jan 30, 2023
Industry
Scientist Pipetting Liquids for Research
New FIX Chromogenic Assay Launched by Precision BioLogic
Jan 18, 2023
Industry
Biomarin Provides Hemophilia A Clinical Development Program Updates
Biomarin Provides Hemophilia A Clinical Development Program Updates
Jan 10, 2023
Industry
Takeda Announces Trial Results on Investigational Therapy for Ultra Rare Blood Disorder
Takeda Announces Trial Results on Investigational Therapy for…
Jan 10, 2023
Industry
Pfizer Announces Trial Updates for Investigational Hemophilia Gene Therapy
Pfizer Announces Trial Updates for Investigational Hemophilia Gene Therapy…
Jan 4, 2023
Industry
Clinical Trial Lab Research
Spark Announces SPK-8011 Updates at ASH
Dec 15, 2022
Industry
BioMarin Shares Community Update for Valoctocogene Roxaparvovec
BioMarin Shares Community Update for Valoctocogene Roxaparvovec
Oct 3, 2022
Industry
Clinical Trial Gene Therapy Double Helix
Recruitment Reopened for Phase 3 AFFINE Gene Therapy Trial
Sep 23, 2022
Industry
Red Blood Cells
FDA Grants Priority Review for Sanofi’s BIVV001
Sep 6, 2022
Industry
Doctor asking questions to patient about care
Rare Factor X Deficiency Survey Shows Disparity in Care
Sep 1, 2022
Industry
BioMarin Presents Abstract on Vector DNA Transmission Risk at ISTH
BioMarin Presents Abstract on Vector DNA Transmission Risk at ISTH
Aug 4, 2022
Industry
New Prophylaxis Approval for REBINYN®
New Prophylaxis Approval for REBINYN®
Aug 3, 2022