NBDF and ATHN Collaboration
NBDF and ATHN Collaboration
The National Bleeding Disorders Foundation and the American Thrombosis & Hemostasis Network Partnering to Create Data Commons.
CSL Presents Three Year Treatment Data for Hemophilia B Gene Therapy
CSL Presents Three Year Treatment Data for Hemophilia B Gene Therapy
The data were presented at the recent 65th American Society of Hematology (ASH) Annual Meeting and Exposition.
FDA Approves Pair of Cell-Based Gene Therapies for Sickle Cell Disease
FDA Approves Pair of Cell-Based Gene Therapies for Sickle Cell Disease
Sickle cell disease is a rare condition that includes a group of inherited blood disorders associated with an abnormality in the hemoglobin protein.
Interview with 2023 NYLI Cohort Member Paxton Mills
Interview with 2023 NYLI Cohort Member Paxton Mills
Paxton Mills is one of the newest members of NYLI, of the 2023 cohort. Paxton has been actively involved in the inheritable blood and bleeding disorders community since her diagnosis with having a rare platelet disorder.
Novo Seven Unavailable in 8 mg Vials Due to Supply Constraints Beginning in January 2024
Novo Seven Unavailable in 8 mg Vials Due to Supply Constraints Beginning in January 2024
Due to supply constraints, Novo Nordisk will be unable to provide the 8 mg vial of NovoSeven® RT from January until mid-2024. Importantly, the overall supply of NovoSeven® RT is expected to remain intact as other vial sizes are available.
FDA Grants Expanded Approval to Wilate® for Prophylaxis in All Types of VWD
FDA Grants Expanded Approval to Wilate® for Prophylaxis in All Types of VWD
Octapharma’s human plasma-derived von Willebrand Factor (VWF)/Factor VIII replacement product Wilate® has been granted expanded approval for prophylaxis by the U.S. Food and Drug Administration (FDA) to include all types of von Willebrand disease (VWD).
First Patient Dosed with Hemophilia Gene Therapy Candidate ASC618
First Patient Dosed with Hemophilia Gene Therapy Candidate ASC618
Investigators of the phase I/II trial are evaluating safety, tolerability, and preliminary efficacy of ASC618.
The Importance of Transgender Health: Interview with Alexis Dinno
The Importance of Transgender Health: Interview with Alexis Dinno
Hemophilia Circle
Hemophilia Memorial at the National AIDS Memorial Grove in Golden Gate Park opened in September 2017