NBDF showcases a wide array of findings from the latest in bleeding disorders research at our annual Bleeding Disorders Conference.
HemoFOCUS Screener for Inattention, Hyperactivity and Impulsivity: A Quality Improvement Intervention for Children with Severe Hemophilia
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Psychosocial Issues
Development of a plasminogen activator 1 (PAI-1) variant to modulate bleeding
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Biomedical/Coagulation Research
Clinical experience with BIVV001, the first investigational factor VIII (FVIII) therapy to break through the von Willebrand factor (VWF) ceiling in hemophilia A
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Using Photovoice with the Bleeding Disorder Population: A Pilot Project
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Peer Support/Outreach/Integration Models
Three-year efficacy and safety results from a phase 1/2 clinical study of AAV5-hFVIII-SQ gene therapy (valoctocogene roxaparvovec) for severe hemophilia A (BMN 270-201 study)
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Identification of Orthopedic and Genetic Needs Reported by Persons with Type 3/Severe Von Willebrand Disease
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Peer Support/Outreach/Integration Models
Modeling of Daily Administration of N8-GP (ESPEROCT®) vs Standard Half-life FVIII for Patients With Hemophilia A Participating in Sports Activities
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
An evaluation of health utility and quality-of-life in hemophilia: a systematic literature review
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Online CME as a Tool to Increase Clinicians’ Knowledge of Clinical Trial Data for Gene Therapy in Hemophilia
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Increasing Medical Alert Devices (MAD) Compliance in School Age Children with Hemophilia: A Quality Improvement Project
AWARDED/PRESENTED: 2019
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Pharmacokinetics, Efficacy, and Safety of High-Purity Factor X for Prophylactic Treatment of Hereditary Factor X Deficiency
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Bringing families affected by Factor XIII deficiency together for a novel educational program
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Peer Support/Outreach/Integration Models
Integrated efficacy and safety analysis of Phase 2 and 3 studies with glecaprevir/pibrentasvir in patients with a history of bleeding disorders and chronic hepatitis C virus genotype 1–6-infection
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Joint health in patients with hemophilia A: analysis from the CHOICE survey
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Bypassing agent (BPA) use for the treatment of bleeds in persons with Hemophilia A (PwHA) with inhibitors before and after emicizumab prophylaxis in the HAVEN 1 study
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Long-term clinical outcomes of rFIXFc prophylaxis in adults 50 years of age or older with severe hemophilia B
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
BAY 94-9027 Maintains Hemostasis During Major Surgery in Adults and Adolescents With Severe Hemophilia A: PROTECT VIII Results
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Head-to-head pharmacokinetic comparisons of N9-GP with standard FIX and rFIXFc in patients with hemophilia B
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Effective Long-term Prophylaxis with BAY 94-9027 in Previously Treated Children: Interim Results of the PROTECT VIII Kids Extension Study
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
PiggyBac mediated gene transfer for prevention of anti-factor VIII antibodies in hemophilia A
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Biomedical/Coagulation Research