NBDF showcases a wide array of findings from the latest in bleeding disorders research at our annual Bleeding Disorders Conference.
Long-term clinical outcomes of rFVIIIFc prophylaxis in adults 50 years of age or older with severe hemophilia A
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Achievement of therapeutic levels of factor VIII activity following gene transfer with valoctocogene roxaparvovec (BMN 270): Long-term efficacy and safety results in patients with severe hemophilia A
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Annual Bleed Rates Compared Before and After Changing to Extended Half Life Products in Home Infusion Patients with severe hemophilia
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Long-term Benefit of BAY 81-8973 Prophylaxis in Children With Severe Hemophilia A: Interim Analysis of the LEOPOLD Kids Extension Study
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Impact of hemophilia on employment - Insights from the PROBE Study
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Empowering the Future of Hemophilia Through Swimming (Poster Abstract)
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Psychosocial Issues
Effects of Factor VIII Prophylaxis on Vascular Remodeling and Synovial Gene Expression Changes Associated with Hemarthrosis in FVIII-Deficient Mice
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Biomedical/Coagulation Research
Efficacy of on-demand treatment of bleeding episodes in hemophilia B patients with extended half-life N9-GP in pivotal trials: an in-depth analysis of treatment
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Retrospective review of unplanned hospitalizations and perceived pain in children and adults with a diagnosis of factor ten deficiency receiving home infusions of commercially available factor ten
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
New Products
Persons With Hemophilia Reinforce Their Desire to be More Active: US Findings From an International Patient Survey
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
The Relationship of Hope and Self-Compassion with Quality of Life among Individuals with Bleeding Disorders
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Psychosocial Issues
Inhibitor Teams: building stronger connections and deeper learning
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Peer Support/Outreach/Integration Models
Pharmacokinetics, Efficacy, and Safety of High-Purity Factor X for Prophylactic Treatment of Hereditary Factor X Deficiency
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Bringing families affected by Factor XIII deficiency together for a novel educational program
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Peer Support/Outreach/Integration Models
Integrated efficacy and safety analysis of Phase 2 and 3 studies with glecaprevir/pibrentasvir in patients with a history of bleeding disorders and chronic hepatitis C virus genotype 1–6-infection
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Joint health in patients with hemophilia A: analysis from the CHOICE survey
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Bypassing agent (BPA) use for the treatment of bleeds in persons with Hemophilia A (PwHA) with inhibitors before and after emicizumab prophylaxis in the HAVEN 1 study
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Long-term clinical outcomes of rFIXFc prophylaxis in adults 50 years of age or older with severe hemophilia B
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
BAY 94-9027 Maintains Hemostasis During Major Surgery in Adults and Adolescents With Severe Hemophilia A: PROTECT VIII Results
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Head-to-head pharmacokinetic comparisons of N9-GP with standard FIX and rFIXFc in patients with hemophilia B
AWARDED/PRESENTED: 2018
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials