NBDF showcases a wide array of findings from the latest in bleeding disorders research at our annual Bleeding Disorders Conference.
Factors influencing uptake of evaluation among hemophilia carriers and potential carriers
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Women's Research
Real-World Specialty Pharmacy Dispensation and Expenditures Associated with Prophylactic Regimens Using Standard and Extended Half-Life Recombinant Factor IX Products in Severe Hemophilia B
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
New Products
Patient Reported Outcomes, Burdens and Experiences (PROBE) Study Data Visualization and Analysis
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
The WFH Annual Global Survey: Gender Distribution
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Women's Research
My Life Our Future Genotyping Days: On the Road Again to New Horizons
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Collaboration/Team Models
Lessons Learned in the Assessment of Pain in US Adults With Hemophilia in the Pain, Functional Impairment, and Quality of Life (P-FiQ) Study: Importance of More Formalized Discussions Around Pain in the Comprehensive Care Setting
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Quality of Life/Outcomes Research
Characterization of Women and Girls with Hemophilia Treated in the US from A Claims Database
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Women's Research
Prevalence of gross motor delays in boys with hemophilia ages 4-14: single site study
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Orthopedic and Physical Therapy
Verification of Effective Zika Virus Reduction by Production Steps Used in theManufacture of Plasma-Derived Medicinal Products
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Biomedical/Coagulation Research
A Cumulative Review on Four Decades of Thrombo-Embolic Events Reported with the Use of Activated Prothrombin Complex Concentrate (APCC) in Congenital Haemophilia
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Inhibitors
PROTECT VIII: Can Eligibility for Less-Frequent Prophylaxis Dosing Regimens Be Predicted by Patient Characteristics?
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Efficacy, safety and pharmacokinetics of once-weekly prophylactic emicizumab (ACE910) in pediatric persons (<12 years) with hemophilia A with inhibitors: interim analysis of single-arm, multicenter, open-label, phase 3 study (HAVEN 2)
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Perceptions of Vulnerability, Protective Behaviors, and Reported Stress in Mothers of Sons with Hemophilia
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Psychosocial Issues
Staying on TRAQ: Determining transition readiness from pediatric to adult care in adolescents and young adults with hemophilia
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Efficacy, safety, and pharmacokinetics of a high-purity plasma-derived factor X (pdFX) concentrate in the prophylaxis of bleeding episodes in children <12 years with moderate to severe congenital factor X deficiency (FXD)
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Fitusiran, an Investigational RNAi Therapeutic Targeting Antithrombin for the Treatment of Hemophilia A and B with and Without Inhibitors: Interim Results from a Phase 2 Extension Study
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
New Products
Assessing the Availability and Use of Resources to Support Youth with Hemophilia, their Families and Care Teams during Transition to Adult Health Care
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Collaboration/Team Models
Survey Finds Interest in Bleeding Disorder Social Work Specialty Credentialing
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Psychosocial Issues
Physician practice patterns in the US show significant variation in how PK parameters are currently used to personalize care for US hemophilia A patients
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Clinical Research/Clinical Trials
Attitudes and Perspectives on Ankle Function in People with Hemophilia: A Qualitative Study
AWARDED/PRESENTED: 2017
GRANT/PROGRAM:
Bleeding Disorders Conference
Orthopedic and Physical Therapy