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Home
  • Who We Are
    • Our Story
      • Mission & History
      • What We Do
      • What Do We Value?
      • NHF’s Health Equity Efforts
      • Accomplishments
      • Financial Statements
      • NHF Media Newsroom
    • Our Team
      • Staff
      • Board of Directors
      • MASAC
      • Meet the NYLI
      • Nursing Working Group
      • Physical Therapy Working Group
      • Social Work Working Group
    • Our Partners
      • Partners In Progress
      • The ACT Initiative
      • Red Tie Society
      • CDC Coop Agreement
    • Careers
      • What Do We Value?
      • Job Openings
      • Volunteer Opportunities
  • Bleeding Disorders A-Z
    • Overview
      • Fast Facts
      • What is a Bleeding Disorder?
      • History
      • Types of Bleeds
      • Inhibitors
      • Women and Bleeding Disorders
    • Types
      • Hemophilia A
      • Hemophilia B
      • Von Willebrand Disease
      • Other Factor Deficiencies
      • Inherited Platelet Disorders
    • Treatment
      • Comprehensive Medical Care
      • Treatment Guidelines (MASAC)
      • Current Treatments
      • Future Therapies
      • Clinical Trials
    • Healthcare Coverage
      • Choosing an Insurance Plan
      • Private Insurance
      • Public Insurance
      • Health Insurance Toolkit
  • Educational Programs
    • Education
      • Bleeding Disorders Conference
      • Inhibitor Education
      • Online Education
      • Rare Bleeding Disorders
      • Von Willebrand Disease
      • Mental Health
      • Gene and Innovative Therapies
      • Women
      • NHF Educational Programming
    • Training
      • Steps for Living Facilitation Training
      • Youth Leadership (NYLI)
      • Youth International Twinning Partnership
    • Outreach
      • Undiagnosed
      • Guías Culturales
      • Health Equity Working Group
  • Advocacy
    • Federal Priorities
      • Access to Care
      • Federal Programs
      • Medicare
      • Medicaid
      • Blood & Blood Product Safety
      • Make All Copays Count
    • State Priorities
      • Utilization Management
      • Patient Out-of-Pocket Expenses
      • Medicaid
    • How You Can Take Action
      • Register to Vote
      • Washington Days
      • Advocacy Do’s and Don’ts
      • 6 Steps for Grassroots Advocacy
      • Tell Your Story
    • Managed Care & Payers
      • Collaborating on Coverage
      • Quality of Care Guidelines
      • CME/CE Webcast Series
      • Educational Web Portal
      • Quality Improvement & Cost Management
  • Research
    • Research Projects
      • Conducted by NHF
      • Funded by NHF
      • Presented at Our Conference
      • Research Journal Club
    • Fund Your Research
      • Judith Graham Pool Postdoctoral Research Fellowship
      • Career Development Award
      • Bridge Award
      • Innovative Investigator Research Award
      • Jeanne Marie Lusher Diversity Fellowship
      • Nursing Excellence Fellowship
      • Physical Therapy Excellence Fellowship
      • Social Work Excellence Fellowship
    • Community Voices in Research
      • What is CVR?
      • How & Why Should I Participate?
      • Impact on Research
      • Frequently Asked Questions
    • National Research Blueprint
      • What is the National Research Blueprint?
      • Involvement from Across the Community
      • Building on the Blueprint
      • Research Priorities
      • State of the Science Research Summit
  • Healthcare Professionals
    • Guidelines on Care
      • Comprehensive Care
      • MASAC Documents
      • Products Licensed (US)
      • Emergency Management
      • Snapshots of VWD Guidelines
    • Education & Resources
      • BDC: Provider Enduring Web Activity
      • NHF-Takeda Clinical Fellowship Program
      • NHF’s Collaborative Learning Exchange
      • Online Education for Providers
      • Live & Online Learning (Partners)
      • Rare Coagulation Resource Room
      • Peer-reviewed Journals
      • NHF Publications
      • Other Associations
    • Allied Healthcare
      • Nursing
      • Physical Therapy
      • Social Work
  • Community Resources
    • Request Information
      • Contact NHF
      • HANDI - NHF’s Information Resource Center
      • Read Our Publications
      • Subscribe for Email Updates
      • Get HemAware Magazine
      • Newsletter Archive
      • Wednesday Webinar Series
    • Resources Near You
      • NHF Chapters
      • Hemophilia Treatment Centers
      • Clinical Trials
      • Bleeding Disorders Camps
    • Financial Assistance
      • Scholarships
      • Patient Assistance Programs
  • Contact Us
  • Subscribe
  • News
  • Events
  • Give
    • Give Now
      • Make a Donation
      • Give Monthly
      • Honor a Loved One
      • Support Research
      • Why NHF?
      • Physician Partners
    • Other Ways to Give
      • Be a Corporate Partner
      • Donate Your Car
      • Give Stock
      • Make a Planned Gift
      • Create a Will
      • Donor Advised Funds
    • Fundraise for NHF
      • NHF GO
      • Run in a Marathon
      • 2022 United Airlines New York City Half Marathon
      • Create Your Own Fundraiser
      • Fundraise on Facebook
    • Join Us
      • Takeda Shoes
      • Red Tie Soiree
      • Bleeding Disorders Awareness Month
      • Find a Walk
      • For Young Professionals
National Hemophilia Foundation Steps for Living Victory for Women Better You Know Unite for Bleeding Disorders Unite Your Way

Resource Guide

Downloadable resources about gene therapy and innovative therapies for hemophilia and other bleeding disorders.
  1. Home
  2. Bleeding Disorders A-Z
  3. Treatment
  4. Future Therapies
  5. Resource Guide
Consumer Publication
Frequently Asked Questions on Gene Therapy
Insights FAQ
Consumer Publication
Gene Therapy Glossary of Terms
Insights Glossary
Consumer Publication
Gene Therapy – Questions for Your Provider
Gene Therapy – Questions for Your Provider
Consumer Publication
La Terapia Genica: Preguntas para su Proveedor
La Terapia Genica - Preguntas para su Proveedor

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  • Glossary
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Contact us

Brendan Hayes
Brendan Hayes
Director of Education, Innovative Therapies
mail bhayes@hemophilia.org
phone (469) 404-8467

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7 Penn Plaza Suite 1204, New York, NY 10001, United States
212.328.3700
212.328.3777

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